Determined Stoke City fan Paul Parsons has been clocking up the miles as he looks to score for charity after being inspired ...

The Periodic Paralysis Association (PPA) today announced the 2nd annual World Periodic Paralysis Day (WPPD), to be observed March 23, 2026. The global initiative brings together nonprofit ...

Reported Promising Data for TN-201 and TN-401 Gene Therapies in Fourth Quarter of 2025; Additional Data Readouts and Pursuit of Regulatory ...

CEO Jasbir Seehra outlined the company’s development priorities and partnership plans during a presentation at Oppenheimer’s ...

After the FDA’s first-ever public listening meeting on data-sharing in the cell and gene therapy space, new draft guidance ...

Detailed price information for Solid Biosciences Inc (SLDB-Q) from The Globe and Mail including charting and trades.

Leadership today looks different than it did a decade ago. These ten women are building movements, challenging industr ...

Scholar Rock Holding () has held its Q4 earnings call. Read on for the main highlights of the call. Claim 70% Off TipRanks Premium. Unlock hedge fund-level data and powerful inves ...

Bureaucracy's Rot Runs Amok at FDA ...

In 2018, when Nell Choi was 9 years old, she began experiencing symptoms that led to hospitalization and a diagnosis of ...

Several abstracts, including a late-breaking podium presentation and posters, bring forward accumulating long-term efficacy, safety and caregiver-reported insights that deepen understanding of ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, will present at the Muscular Dystrophy Association (MDA) Clinical & Scientific Conference, taking ...