The gene editing treatment targets the relatively common 1717-1G>A splicing mutation, which does not respond to many current CF therapies.

Chance” is amazing. And almost invariably misunderstood. When we think of probability, what often comes to mind is the ...

SYNGAP1 encephalopathy is a rare genetic disorder for which there is no treatment. It causes epilepsy, intellectual ...

SYNGAP1 encephalopathy is a rare genetic disorder for which there is no treatment, causing epilepsy, intellectual disability, psychomotor delay and, frequently, autism.

Though many studies approach the developmental disorder Rett syndrome as a single condition arising from general loss of ...

Remarkably, 98 percent of our DNA does not code for genes. Once considered “junk DNA,” it is now well appreciated that these ...

Some researchers hold that evolution hasn’t much altered humans in the past 10,000 years. A new analysis of ancient DNA ...

Researchers say a new AI system can identify disease-causing mutations and explain their biological effects, potentially ...

In 2025, baby KJ Muldoon became the first person to receive a personalized gene editing treatment, which likely saved his ...

The Aurora Mutation is a special mutation that comes from a weather event. It first appeared in Grow a Garden with the Mega Harvest update on June 28, 2025. On this page, we'll detail the weather ...

Armed with sophisticated chemistry and fresh approaches to drug design, researchers are closing in on innovative strategies to undermine a cancer-causing mutant protein once considered ‘undruggable’.

In Grow a Garden, players can improve a fruit’s appearance and value through different mutations. Some mutations are obtained from pets, weather, and admin events, while others come from special gear.